Tag: ultrarare

Zebrafish mannequin for an ultra-rare genetic illness reveals two promising drug candidates

Credit score: EMBO Molecular Medication (2025). DOI: 10.1038/s44321-025-00204-8 Can a small fish…

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Scientists analyze a number of genetic variants of familial chilomicronemia syndrome, an ultrarare illness

As identified by María José Ariza, researcher of the Lipids and Arteriosclerosis…

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